Monday, October 19, 2009

Inherited Neuromuscular Diseases (book )

Translation from Pathomechanisms to Therapies
Series: Advances in Experimental Medicine and Biology , Vol. 652

Espinós, Carmen; Felipo, Vicente; Palau, Francesc (Eds.)

2009, XIII, 304 p., Hardcover

ISBN: 978-90-481-2812-9

Keywords: muscular dystrophies, mitochondrial disorders, peripheral neuropathies, spinal muscular atrophy, motoneurone disease, Friedreich ataxia, genetics, neuromuscular disorders, peripheral nervous system, cellular biology, pathomechanisms, therapies and treatments.

Idebenone Appears Safe in Patients With Friedreich's Ataxia: Presented at ANA

Doctor's Guide Publishing Limited.

Presentation title: SNT-MC17/Idebenone to Treat Friedreich's Ataxia: Preliminary Phase 3 Safety Data. Poster T-80]

Keywords: blinded interim safety analysis, Friedreich's ataxia, clinical trial, idebenone, severe events, supraventricular extrasystole, reduced visual acuity, fatigue, anxiety, flatulence/abdominal discomfort, electrocardiograms, vital signs, laboratory test, SNT-MC17, headache, nausea, diarrhoea, vomiting, abdominal pain, upper abdominal pain, fatigue, hypercholesterolaemia, rash, flatulence, pruritus.