Friedreich Ataxia Scientific News
Friedreich Ataxia and close related scientific news. Topics related to rare diseases.
Thursday, May 2, 2024
Genetic Determined Iron Starvation Signature in Friedreich's Ataxia
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Grander, M., Haschka, D., Indelicato, E., Kremser, C., Amprosi, M., Nachbauer, W., Henninger, B., Stefani, A., Högl, B., Fischer, C., Seifer...
One-to-one Benefit provided by Antioxidants to cultured skin Fibroblasts from Friedreich Ataxia patients
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One-to-one Benefit provided by Antioxidants to cultured skin Fibroblasts from Friedreich Ataxia patients, Paule Bénit, Malgorzata Rak, Pierr...
Astellas' Friedreich’s ataxia gene therapy cleared for clinical study after earlier version stumbled
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April 25, 2024. Astellas' Friedreich’s ataxia gene therapy cleared for clinical study after earlier version stumbled. On Thursday, the J...
Alterity Therapeutics Presents New Data Demonstrating Potential of ATH434 to Treat Rare Neurodegenerative Disease Friedreich’s Ataxia
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MELBOURNE, Australia and SAN FRANCISCO, April 29, 2024 (GLOBE NEWSWIRE) -- Alterity Therapeutics (ASX: ATH, NASDAQ: ATHE) (“Alterity” or “th...
Opinion: Larimar Could Compete with Biogen in Friedreich’s Ataxia
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BioSpace. Published: Apr 29, 2024. n February 2024, Larimar Therapeutics released positive Phase II data for its injectable subcutaneous inv...
Inherited metabolic disorders in Cyprus
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Theodoros Georgiou, Petros P. Petrou, Anna Malekkou, Ioannis Ioannou, Marina Gavatha, Nicos Skordis, Paola Nicolaidou, Irini Savvidou, Emili...
Wednesday, May 1, 2024
Mitochondria function in cytoplasmic FeS protein biogenesis
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Andrew Dancis, Ashutosh K. Pandey, Debkumar Pain, Mitochondria function in cytoplasmic FeS protein biogenesis, Biochimica et Biophysica Acta...
Tuesday, April 30, 2024
Frataxin deficiency in proprioceptive neurons is causal to inflammatory and glial responses in dorsal root ganglia
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Frataxin deficiency in proprioceptive neurons is causal to inflammatory and glial responses in dorsal root ganglia, Pauline Meriau, Laure We...
Deciphering the mechanisms of gene silencing induced by triplet-repeat expansions
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Deciphering the mechanisms of gene silencing induced by triplet-repeat expansions. Nat. Plants (2024). doi:10.1038/s41477-024-01673-4 A tri...
Frataxin deficiency shifts metabolism to promote reactive microglia via glucose catabolism
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NEWS PROVIDED BY Life Science Alliance - New York April 17, 2024 Immunometabolism investigates the intricate relationship between the immune...
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