Wednesday, August 12, 2015

PATENT: SMALL MOLECULE ACTIVATORS OF MITOCHONDRIAL FUNCTION

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NEW PATENT: SMALL MOLECULE ACTIVATORS OF MITOCHONDRIAL FUNCTION. Inventor(s): WILSON ROBERT B [US]; COTTICELLI MARIA GRAZIA [US]; BENEDETT...
Saturday, August 8, 2015

Key Patent Granted For AAVLife’s Gene-Therapy Program to Treat Cardiomyopathy in Friedreich’s Ataxia

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Key Patent Granted For AAVLife’s Gene-Therapy Program to Treat Cardiomyopathy in Friedreich’s Ataxia . BUSINESS WIRE, August 05, 2015 The ...
Monday, August 3, 2015

The quality of economic evaluations of ultra-orphan drugs in Europe – a systematic review

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The quality of economic evaluations of ultra-orphan drugs in Europe – a systematic review . Y. Schuller, C. E. M. Hollak and M. Biegstraaten...
Friday, July 31, 2015

Friedreich Ataxia in Classical Galactosaemia

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Friedreich Ataxia in Classical Galactosaemia . Siobhán Neville, Siobhan O’Sullivan, Bronagh Sweeney, Bryan Lynch, Donncha Hanrahan, Ina Kne...

Friedreich’s Ataxia Research Collaboration Announced

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Friedreich’s Ataxia Research Collaboration Announced . Medical Sciences Division, University of Oxford, 30 July 2015. A new collaborative ...
Tuesday, July 28, 2015

Les médicaments orphelins : des opportunités méconnues pour les développeurs en Europe

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Les médicaments orphelins : des opportunités méconnues pour les développeurs en Europe . Orphan Drugs: Underrated Opportunities for The Deve...
Sunday, July 26, 2015

Mitigation of Myocardial Ischemia-Reperfusion Injury via HIF-1α-Frataxin Signalling.

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Mitigation of Myocardial Ischemia-Reperfusion Injury via HIF-1α-Frataxin Signalling. Nelson Amaral, Darlington Okonko; American Journal of ...

Resources, challenges and way forward in rare mitochondrial diseases research.

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Resources, challenges and way forward in rare mitochondrial diseases research. Rajput NK, Singh V and Bhardwaj A. [v1; ref status: indexed...
Thursday, July 23, 2015

L'atàxia de Friedreich: estudi del dèficit de frataxina en miòcits cardíacs

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Friedreich's ataxia: a study of frataxin deficiency in cardiac myocytes . Author: Èlia Obis Monné, Director: Jordi Tamarit Sumalla, Joaq...

RNA-based drugs, very promising research (RaNA Therapeutics)

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RNA-based drugs, very promising research (RaNA Therapeutics) . EXOME News, Ben Fidler July 23rd, 2015 and The Boston Globe (Bussines)  by J...