Wednesday, June 30, 2021

LEXEO Therapeutics Receives Rare Pediatric Disease Designation and Orphan Drug Designation for LX2006 for the Treatment of Friedreich’s Ataxia

›
NEW YORK, June 30, 2021 (GLOBE NEWSWIRE) -- LEXEO Therapeutics, a clinical-stage gene therapy company, today announced that the U.S. Food an...
Tuesday, June 29, 2021

Generation of transgene-free iPSC lines from three patients with Friedreich’s ataxia (FRDA) carrying GAA triplet expansions in the first intron of FXN gene

›
Simge Kelekçi, Deniz Uğurlu-Çimen, Deniz Ata, Burcu Özçimen, Abdullah Burak Yıldız, Mehmet Batuhan Karakuş, Esra Börklü Yücel, Tamer T. Önde...
Monday, June 28, 2021

Friedreich Ataxia: Multidisciplinary Clinical Care

›
Lynch DR, Schadt K, Kichula E, McCormack S, Lin KY., J Multidiscip Healthc 2021;14:1645-1658 doi:10.2147/JMDH.S292945  This review provides...
Sunday, June 20, 2021

The cardiomyopathy of Friedreich's ataxia common in a family: A case report

›
Amini O, Lakziyan R, Abavisani M, Sarchahi Z. Ann Med Surg (Lond). 2021 May 24;66:102408. doi: 10.1016/j.amsu.2021.102408.  Because early di...
Thursday, June 17, 2021

New biotech kid on the block making news

›
June 17, 2021. Capsida Biotherapeutics, a Newbury Park-based startup that recently raised $140 million in Series A funding, is partnering wi...

Inicio Ronda de Inversión Biointaxis con Capital Cell

›
06.17.2021. Biointaxis es una spin-off biotecnológica surgida del Instituto de Investigación Germans Trias i Pujol (IGTP) y del grupo farmac...
Wednesday, June 16, 2021

CRISPR Therapeutics and Capsida Biotherapeutics Announce Strategic Collaboration to Develop Gene-Edited Therapies for Amyotrophic Lateral Sclerosis and Friedreich’s Ataxia

›
ZUG, Switzerland and CAMBRIDGE, Mass. and THOUSAND OAKS, Calif., June 15, 2021 (GLOBE NEWSWIRE) -- CRISPR Therapeutics (Nasdaq: CRSP), a bio...
Tuesday, June 15, 2021

A pathogenic role for histone H3 copper reductase activity in a yeast model of Friedreich's Ataxia

›
Oscar A Campos, Narsis Attar, Nathan V Mallipeddi, Chen Cheng, Maria Vogelauer, Stefan Schmollinger, Sabeeha S Merchant, Siavash K Kurdistan...
Monday, June 14, 2021

Evaluation of the Effect of Artesunate in Friedreich Ataxia (FA) (ARTEMIS)

›
ClinicalTrials.gov Identifier: NCT04921930; Sponsor: Institut National de la Santé Et de la Recherche Médicale, France Collaborator: Imagine...
Saturday, June 12, 2021

Automatic speech recognition in neurodegenerative disease

›
Authors: Benjamin G. Schultz, Venkata S. Aditya Tarigoppula, Gustavo Noffs, Sandra Rojas, Anneke van der Walt, David B. Grayden, Adam P. Vog...