Monday, October 6, 2025

357PLong-term vatiquinone treatment slows Friedreich’s ataxia disease progression relative to FACOMS natural history

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357PLong-term vatiquinone treatment slows Friedreich’s ataxia disease progression relative to FACOMS natural history. Vagabov, A. et al. Neu...

234PLong-term use of omaveloxolone in patients with Friedreich ataxia: up to 5 years of natural history propensity score matching from the MOXIe OLE

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234PLong-term use of omaveloxolone in patients with Friedreich ataxia: up to 5 years of natural history propensity score matching from the M...

Friedreich Ataxia and Related Diabetes: Therapeutic Approach Targeting Mitochondrial Dysfunction

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Pichakacheri Sureshkumar, Sidharth S Kumar, Johny Cheriyan, Asif Masood, Friedreich Ataxia and Related Diabetes: Therapeutic Approach Target...

357P Long-term vatiquinone treatment slows Friedreich’s ataxia disease progression relative to FACOMS natural history

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A. Vagabov, J. Cherry, A. Duqette, M. França, S. Perlman, A. Durr, E. Bertini, K. Mathews, L. Schöls, A. Fournier, M. Delatycki, S. Subramon...
Saturday, October 4, 2025

Emerging therapies for Friedreich Ataxia and the prospect of future combination treatments

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Lees, J. G., Li, L., & Lim, S. Y. (2025). Emerging therapies for Friedreich Ataxia and the prospect of future combination treatments. Fu...
Wednesday, October 1, 2025

Larimar Therapeutics Announces Positive Data from Ongoing Long-term Open Label Study and Updates to Nomlabofusp Program for Friedreich’s Ataxia

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BALA CYNWYD, Pa., Sept. 29, 2025 (GLOBE NEWSWIRE) -- Larimar Therapeutics, Inc. (Larimar) (Nasdaq: LRMR), a clinical-stage biotechnology com...
Friday, September 26, 2025

Friedreich's Ataxia in Colombia: A Population-Based Study of Incidence and Socioeconomic Determinants

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Correa-Arrieta C, Castellar-Leones S, Ruiz-Ospina E, Villamil-Osorio M, Bobadilla-Quesada EJ, Ortiz-Corredor F. Friedreich's Ataxia in C...

Impact of age on neurofilament light chain in Friedreich ataxia: a 1-year longitudinal study

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Petrillo S, Mongelli A, Castaldo A, Sarro L, Azzarelli S, Ronco R, Castellotti B, Gellera C, Piemonte F, Mariotti C. Impact of age on neurof...

Leriglitazone improves iron homeostasis and ferroptotic markers in frataxin-deficient dorsal root ganglia neurons

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Biomed Pharmacother . 2025 Sep 18:192:118553. doi: 10.1016/j.biopha.2025.118553. Online ahead of print. Leriglitazone improves iron homeosta...

Type and position of repeat interruptions as determinants of disease severity and expansion size in Friedreich ataxia

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Type and position of repeat interruptions as determinants of disease severity and expansion size in Friedreich ataxia, Benkirane, Mehdi et a...