Friedreich Ataxia Scientific News
Friedreich Ataxia and close related scientific news. Topics related to rare diseases.
Saturday, June 5, 2021
Rescue of central and peripheral neurological phenotype of friedreich's ataxia by intravenous delivery
Application US16/651,617- Assigned to VOYAGER THERAPEUTICS, INC.
Described herein are compositions and methods for treating Friedreich's Ataxia (FA) using adeno-associated virus (AAV) to deliver therapeutics agents.
Rescue of central and peripheral neurological phenotype of friedreich's ataxia by intravenous delivery
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