Wednesday, April 30, 2025

Progression of Friedreich Ataxia to Scoliosis and Cardiomyopathy: Utility of Real-World Data From Medical Claims (P12-5.032)

Progression of Friedreich Ataxia to Scoliosis and Cardiomyopathy: Utility of Real-World Data From Medical Claims (P12-5.032) April 8, 2025 issue 104 (7_Supplement_1) doi:10.1212/WNL.0000000000210504 

 Real-world data from medical claims can augment evidence from natural history studies in FA to allow for analyses of a broader range of commercially insured patients and explore patient characteristics, practice patterns, and outcomes not currently available.