Translating the Genomics Revolution: The Need for an International Gene Therapy Consortium for Monogenic Diseases

Translating the Genomics Revolution: The Need for an International Gene Therapy Consortium for Monogenic Diseases. Jacques P Tremblay, Xiao Xiao, Annemieke Aartsma-Rus, Carlos Barbas, Helen M Blau, Adam J Bogdanove, Kym Boycott, Serge Braun, Xandra O Breakefield, Juan A Bueren, Michael Buschmann, Barry J Byrne, Michele Calos, Toni Cathomen, Jeffrey Chamberlain, Marinee Chuah, Kenneth Cornetta, Kay E Davies, J George Dickson, Philippe Duchateau, Terence R Flotte, Daniel Gaudet, Charles A Gersbach, Renald Gilbert, Joseph Glorioso, Roland W Herzog, Katherine A High, Wenlin Huang, Johnny Huard, J Keith Joung, Depei Liu, Dexi Liu, Hanns Lochmüller, Lawrence Lustig, Jeffrey Martens, Bernard Massie, Fulvio Mavilio, Jerry R Mendell, Amit Nathwani, Katherine Ponder, Matthew Porteus, Jack Puymirat, Jude Samulski, Shin’ichi Takeda, Adrian Thrasher, Thierry VandenDriessche, Yuquan Wei, James M Wilson, Steve D Wilton, John H Wolfe and Guangping Gao; Molecular Therapy (2013); 21 2, 266–268. doi:10.1038/mt.2013.4

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Jacques P Tremblay, Centre de Recherche du CHU and Department of Molecular Medicine, Université Laval, Quebec, Quebec, Canada, is working on gene therapy and protein replacement therapy in Friedreich's ataxia since long time.

See also: Translating the Genomics Revolution . (Jacques P Tremblay)