Cell Symposia: Using Stem Cells to Model and Treat Human Disease

Cell Symposia: Using Stem Cells to Model and Treat Human Disease, November 21-23, 2013, Cedars-Sinai Medical Center, Los Angeles, USA

Posters about Friedreich's Ataxia

Combined genome editing, reprogramming, and high-throughput biology identify novel therapeutics for Friedreich’s Ataxia
R. Villaseñor*1 ,2, L. Miraglia3, P. Manos4, F. Berenshteyn4, A. Romero3, B. Tu3, T. Punga1 ,2, P. Knuckles1 ,2, S. Duss1 ,2, C. Littlefield4, 1Friedrich Miescher Institute for Biomedical Research, Switzerland, 2University of Basel, Switzerland, 3Genomics Institute of the Novartis Research Foundation, USA, 4Novartis Institutes for Biomedical Research, USA

Epigenetic therapy for Friedreich’s ataxia
E. Soragni*1, E. Campau1, J. Du1, W. Miao2, V. Jacques2, J.R. Rusche2, J.M. Gottesfeld1, 1The Scripps Research Institute, USA, 2Repligen Corporation, USA

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