A pilot trial of deferiprone for neurodegeneration with brain iron accumulation.

Haematologica. 2011 Jul 26. [Epub ahead of print]

Abbruzzese G, Cossu G, Balocco M, Marchese R, Murgia D, Melis M, Galanello R, Barella S, Matta G, Ruffinengo U, Bonuccelli U, Forni GL.

(Clinicaltrials.gov identifier: NTC00907283.)

Keywords: Deferiprone, Friedreich's ataxia, cerebral iron accumulation, pantothenate kinase-associated neurodegeneration, parkinsonism and focal dystonia, Magnetic resonance imaging, neurological examinations, Chelation treatment.