Erythropoietin in friedreich ataxia: No effect on frataxin in a randomized controlled trial

Movement Disorder, Article first published online: 4 JAN 2012 | DOI: 10.1002/mds.24066
Caterina Mariotti, Roberto Fancellu, Serena Caldarazzo, Lorenzo Nanetti, Daniela Di Bella, Massimo Plumari, Giuseppe Lauria, Maria D. Cappellini, Lorena Duca, Alessandra Solari and Franco Taroni

Results: Erythropoietin treatment was safe and well tolerated, but did not result in any significant hematological, clinical, or biochemical effects in Friedreich ataxia patients.