The State of Gene Therapies: The FDA Perspective

The State of Gene Therapies: The FDA Perspective, Molecular Therapy (2012); 20 5, 877–878. doi:10.1038/mt.2012.51, Daniel Takefman and Wilson Bryan Full Text.

Keywords: Clinical development of gene therapy, 320 ongoing gene therapy clinical trials, Office of Cellular Tissue and Gene Therapies (OCTGT), Center for Biologics Evaluation and Research of the US Food and Drug Administration (FDA), treatments for specific, well-defined genetic disorders ... Full Text.