Accelerating development, registration and access to medicines for rare diseases in the European Union through adaptive approaches: features and perspectives

Accelerating development, registration and access to medicines for rare diseases in the European Union through adaptive approaches: features and perspectives. David Uguen, Thomas Lönngren, Yann Le Cam, Sarah Garner, Emmanuelle Voisin, Carlo Incerti, Marc Dunoyer and Moncef Slaoui; Orphanet Journal of Rare Diseases 2014, 9:20 doi:10.1186/1750-1172-9-20

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