GoFAR reinforces partnership with Powell Gene Therapy Center at University of Florida (UF) to develop a gene therapy for Friedreich’s ataxia

Torino-Italia, April 20-2018. In January, GoFAR awarded an additional grant of $450,000 to Manuela Corti, P.T., Ph.D., assistant professor of Dr. Barry Byrne M.D., Ph.D director of the UF Powell Gene Therapy Center. GoFAR originally began a collaboration with the UF Powell Gene Therapy Center in 2016 to develop AVV-mediated gene therapy for FA awarding a grant of $750,000.The total award of $1.2Ml has been staged to reach milestones toward the clinical implantation of the therapeutic strategy for FA. The most recent award will be used to complete preclinical studies and prepare data for submission to the U.S. Food and Drug Administration (FDA), the European Medicines Agency (EMA), and the Italian regulatory authority, Instituto Superiore della Sanità (ISS). Hopefully trials are expected to begin later this year.

International advocacy group GoFAR funds UF Health research for Friedreich’s ataxia gene therapy program


GoFAR reinforces partnership with Powell Gene Therapy Center at University of Florida (UF) to develop a gene therapy for Friedreich’s ataxia