CAMBRIDGE, Mass., May 18, 2018 (GLOBE NEWSWIRE) -- Voyager Therapeutics, Inc. (NASDAQ:VYGR), a clinical-stage gene therapy company focused on developing life-changing treatments for severe neurological diseases today announced additional data presentations at the American Society of Gene and Cell Therapy (ASGCT) taking place May 16-19, 2018, in Chicago, Ill.
Oral Presentation Title: "Rescue of Central and Peripheral Neurological Phenotype in a Mouse Model of Friedreich's Ataxia by Intravenous Delivery of AAV Frataxin with a Novel Capsid" Abstract O672.
Data presented at this year's ASGCT meeting demonstrated in a transgenic mouse model of FA, that one-time, post-symptomatic IV dosing of Voyager's vector composed of a novel AAV capsid and a frataxin transgene durably improved motor function and rescued the FA phenotype based on multiple functional tests of sensory and motor behavior.
Voyager Therapeutics Announces Additional Data at the American Society of Gene and Cell Therapy 2018 Annual Meeting