Patient reported outcomes in Friedreich's Ataxia after withdrawal from Idebenone

Cook, A. , Boesch, S. , Heck, S. , Brunt, E. , Klockgether, T. , Schöls, L. , Schulz, A. and Giunti, P. (2019). Acta Neurol Scand. Accepted Author Manuscript. doi:10.1111/ane.13088

This study provides no data to suggest that FRDA patients could correctly determine their treatment assignment over a 2‐month period. We hope that this study design will help inform future trials so that patients’ experiences of symptoms are more reliably measured.

Patient reported outcomes in Friedreich's Ataxia after withdrawal from Idebenone