Although no single therapy has yet delivered a cure, the growing understanding of FRDA’s underlying mechanisms, coupled with an expanding therapeutic arsenal and more refined clinical measures, offers genuine hope that transformative, life-changing treatments are within reach. Realizing this promise will depend on continued collaboration among patients, clinicians, researchers, industry, and regulatory stakeholders to ensure that scientific advances translate into tangible, meaningful benefits for the FRDA community.
Saturday, October 4, 2025
Emerging therapies for Friedreich Ataxia and the prospect of future combination treatments
Lees, J. G., Li, L., & Lim, S. Y. (2025). Emerging therapies for Friedreich Ataxia and the prospect of future combination treatments. Future Rare Diseases, 5(1). doi:10.1080/23995270.2025.2563497
