OLIGOTHERAPEUTIC STRATEGIES FOR THE TREATMENT OF FRIEDREICH’S ATAXIA

OLIGOTHERAPEUTIC STRATEGIES FOR THE TREATMENT OF FRIEDREICH’S ATAXIA. F. Ozsolak, D. Jun Li, D. Parekh, D. Knowlton, M. Wysk, R. Subramanian, J. Barsoum RaNA Therapeutics. Poster 2269T. American Society of Human Genetics (ASHG) 2013 Annual Meeting, Octubre, 22-26, Boston.

KEYWORDS: Friedreich’s ataxia (FRDA), frataxin (FXN), non-coding RNA (ncRNA), oligonucleotide-based therapeutic approaches.