Multiple trials have been conducted in subjects with FRDA in recent years, and our search yielded seven publications since 2018, assessing six different drugs. Most trials used the Friedreich Ataxia Rating Scale (FARS) or modified FARS (mFARS), 9-hole peg test (9HPT), and 25 or 8 min walk tests to assess the efficacies of the drugs. However, none of these tests are specific to neuropathy progression.
Monday, July 10, 2023
Novel Therapeutic Approaches in Inherited Neuropathies: A Systematic Review
Hustinx M, Shorrocks AM, Servais L. Novel Therapeutic Approaches in Inherited Neuropathies: A Systematic Review. Pharmaceutics. 2023 May;15(6):1626. DOI: 10.3390/pharmaceutics15061626. PMID: 37376074; PMCID: PMC10305260.
